Search results (5)
« Back to PublicationsRecent developments in gene therapy for Parkinson's disease.
Journal article
Szunyogh S. et al, (2025), Mol Ther, 33, 2052 - 2064
Drug repurposing in amyotrophic lateral sclerosis (ALS).
Journal article
Carroll E. et al, (2025), Expert Opin Drug Discov, 20, 447 - 464
Dynactin-1 mediates rescue of impaired axonal transport due to reduced mitochondrial bioenergetics in amyotrophic lateral sclerosis motor neurons.
Journal article
Dafinca R. et al, (2024), Brain Commun, 6
C9orf72-ALS human iPSC microglia are pro-inflammatory and toxic to co-cultured motor neurons via MMP9.
Journal article
Vahsen BF. et al, (2023), Nat Commun, 14
Targeting phosphoglycerate kinase 1 with terazosin improves motor neuron phenotypes in multiple models of amyotrophic lateral sclerosis.
Journal article
Chaytow H. et al, (2022), EBioMedicine, 83

