Generation and LDLR Functional Correction of Familial Hypercholesterolemia iPSC With Physiologically Responsive Non-Integrating BAC Vector

Ramakrishnan VM., Yang JY., Burchell P., Tien KT., Bocard BR., Maijub JG., Williams SK., Wade-Martins R., West FD., Boyd NL.

Type

Conference paper

Publication Date

2014

Volume

130

Keywords

Stem cell therapy, Atherosclerosis, LDL, Cholesterol, Hyperlipidemia

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