Modelling amyotrophic lateral sclerosis (ALS) using mutant and CAS9/CRISPR-corrected motor neurons from patients with C9ORE72 mutations reveals disease-specific cellular phenotypes

Mutihac R., Ababneh N., Scaber J., Wade-Martins R., Cowley S., Talbot K.

DOI

10.1016/j.jns.2015.08.198

Type

Conference paper

Publication Date

2015

Volume

357

Pages

E48 - E48

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