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Oral Glucosamine Ameliorates Aggravated Neurological Phenotype in Mucopolysaccharidosis III Type C Mouse Model Expressing Misfolded HGSNAT Variant
Pan X., Taherzadeh M., Bose P., Heon-Roberts R., Nguyen ALA., Xu T., Pará C., Yamanaka Y., Priestman DA., Platt FM., Khan S., Fnu N., Tomatsu S., Morales CR., Pshezhetsky AV.
DOI
10.1101/2021.08.26.457793
Type
Preprint
Publication Date
2021-08-27T00:00:00+00:00