Postdoctoral Research Scientist
Transfer of genetic therapy across human populations: molecular targets for increasing patient coverage in repeat expansion diseases.
Varela MA. et al, (2016), Eur J Hum Genet, 24, 271 - 276
Identification of sequences common to more than one therapeutic target to treat complex diseases: simulating the high variance in sequence interactivity evolved to modulate robust phenotypes.
Varela MA., (2015), BMC Genomics, 16
Prevention of exercised induced cardiomyopathy following Pip-PMO treatment in dystrophic mdx mice.
Betts CA. et al, (2015), Sci Rep, 5
Corrigendum: Cross-talking noncoding RNAs contribute to cell-specific neurodegeneration in SCA7.
Tan JY. et al, (2015), Nat Struct Mol Biol, 22
Correlating In Vitro Splice Switching Activity With Systemic In Vivo Delivery Using Novel ZEN-modified Oligonucleotides.
Hammond SM. et al, (2014), Mol Ther Nucleic Acids, 3