Small molecule utrophin modulators for the therapy of Duchenne muscular dystrophy (DMD)
Russell A., Vuorinen A., Willis N., Conole D., Chatzopoulou M., Emer E., Wilkinson I., Davies S., Guiraud S., Squire S., Babbs A., Dugdale H., Edwards B., Hemming S., Moir L., Perkins K., Harriman S., Wilson F., Wynne G., Tinsley J., Davies K.