Modified Patient Stem Cells as Prelude to Autologous Treatment of Muscular Dystrophy
Davies KE., Grounds MD.
Duchenne muscular dystrophy is a devastating muscle wasting disease for which there is no effective treatment. In this issue of Cell Stem Cell, Benchaouir et al. (2007) demonstrate the delivery of genetically corrected CD133+ patient cells into mice, suggesting a new potential avenue for autologous cell therapy. © 2007 Elsevier Inc. All rights reserved.